Register for the 2022 Clinical and Scientifc Conference

 

ALL CONFERENCE SESSION TIMES LISTED ARE IN CENTRAL STANDARD TIME

6:00 PM – 8:00 PM

Welcome Reception in Exhibit Hall

Add to Calendar3/13/2022 06:00 PM4/13/2022 10:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
7:00 AM – 8:00 AM

Industry Forum Breakfast Sponsored by Edgewise
Industry Forum Breakfast Sponsored by NS Pharma

Add to Calendar3/14/2022 07:00 AM3/14/2022 8:00 AMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
8:30 AM - 9:30 AM

Opening and Keynote Address

Add to Calendar3/14/2022 08:30 AM3/14/2022 9:30 AMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
10:00 AM – 8:00 PM

Exhibit Hall and Poster Sessions Open

Add to Calendar3/14/2022 10:00 AM3/14/2022 8:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
10:00 AM – 12:00 PM

NMD Registry Data Moderated Panel Discussion: MDStarNet, MOVR, PPMD, MDF, ASTDR, CureSMA

Add to Calendar3/14/2022 10:00 AM3/14/2022 12:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
12:00 PM – 01:30 PM

Industry Forum Lunch Sponsored by Biogen
Industry Forum Lunch Sponsored by Pfizer
Industry Forum Lunch Sponsored by Sarepta

Add to Calendar3/14/2022 07:00 AM3/14/2022 8:00 AMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
1:30 PM – 2:30 PM

Lab to Life: LGMD

Speaker ImageNicolas Johnson, MD, MS-CI (Chair)


Session will review advances in translational research in LGMD. Speakers will discuss steps to improve genetic diagnosis, development of small molecules, and advances in gene replacement therapy.

Add to Calendar3/14/2022 01:30 PM4/14/2022 2:30 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
1:30 PM – 3:30 PM

New Gene Discoveries in NMD

(CME Accredited Session)
Speaker ImageAlan Beggs, PhD (Chair)

Add to Calendar3/14/2022 01:30 PM3/14/2022 3:30 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
2:30 PM – 3:30 PM

Lab to Life: FSHD

Speaker ImageJeffrey Statland, MD (Chair)


Session explores implementation of targeted therapies in clinical trials, our molecular understanding of FSHD, and how we measure changes in future clinical trials

Add to Calendar3/14/2022 02:30 PM3/14/2022 3:30 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
4:00 PM - 5:00 PM

Lab to Life: MG

Speaker ImageHenry Kaminski, MD (Chair)


Session will review the journey of treatment to patient from identification of unmet need to prescription of the drug and access for all patients.

Add to Calendar3/14/2022 04:00 PM3/14/2022 5:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
4:00 PM - 5:00 PM

Functional/PROs/Composite Clinical Trial Endpoints in DMD

(CME Accredited Session)
Speaker ImageDr. Erik Henricson, PhD, MPH (Chair)


Session will explore uses and intersections between clinically reported outcome tools, person-reported outcome tools, and single- and multi-domain composite endpoints in DMD clinical research.

Add to Calendar3/14/2022 04:00 PM3/14/2022 5:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
5:00 PM – 6:00 PM

Lab to Life: Congenital Myopathies/Dystrophies

Speaker ImageChamindra Konersman, MD (Chair)


Session will explore the disease spectrum, genetics, and phenotypic complexity of congenital myopathies and muscular dystrophies, as well as current and future strategies for disease modifying treatments, and preparing for meaningful clinical trial outcome measures.

Add to Calendar3/14/2022 05:00 PM3/14/2022 6:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
5:00 PM – 6:00 PM

Updates in Respiratory Care in NMD

(CME Accredited Session)
Speaker ImageBrad Troxler, MD (Chair)


Session will provide a forum to learn about the latest advancements in respiratory care for patients with NMD. Use of advanced airway clearance techniques and positive airway pressure devices will be discussed. The impact of respiratory care on patient with NMD will be shared.

Add to Calendar3/14/2022 05:00 PM3/14/2022 6:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
6:00 PM – 8:00 PM

Poster & Networking Reception

Add to Calendar3/14/2022 06:00 PM3/14/2022 8:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
7:00 AM – 8:00 AM

Industry Forum Breakfast Sponsored by Amylyx
Industry Forum Breakfast Sponsored by Fulcrum

Add to Calendar3/15/2022 07:00 PM3/15/2022 8:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
8:30 AM - 10:00 AM

Mitochondrial Interventions: Small Molecule and Gene Therapy

This session will explore a few approaches with great clinical potential that use small molecules or genetic manipulation.

Add to Calendar3/15/2022 08:30 AM3/15/2022 10:00 AMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Promoting Diversity in Research

Speaker ImageSusan Apkon, MD (Chair)


Session will provide a greater understanding of the barriers to participation in clinical research for patients from diverse backgrounds and opportunities to improve their involvement. Panelists will share their diverse experience and perspectives as clinicians, family members, and industry partners.

Add to Calendar3/15/2022 08:30 AM3/15/2022 10:00 AMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Telehealth Learnings in Clinical Care and Research: Learnings from the Pandemic

(CME Accredited Session)
Speaker ImageDustin Nowacek, MD (Chair)


Session will discuss telehealth experiences, identify the benefits, and recognize limits of virtual care.

Add to Calendar3/15/2022 08:30 AM3/15/2022 10:00 AMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Ethical Considerations in NMD

(CME Accredited Session)
Speaker ImageJohn Brandsema, MD (Chair)


Moderated panel discussion of cases that have been complicated ethically and generate an open forum for discussion of how to best navigate similar situations when they arise.

Add to Calendar3/15/2022 08:30 AM3/15/2022 10:00 AMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
10:00 AM – 8:00 PM

Exhibit Hall and Poster Sessions Open

Add to Calendar3/15/2022 10:30 AM3/15/2022 8:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
10:30 AM – 12:00 PM

Pediatric CMT

(CME Accredited Session)
Speaker ImageMichael Shy, MD (Chair)


Session will provide an update on natural history studies, a description of pediatric patient-reported outcomes assessment evaluating the self-reported quality of life for children with CMT, approaches to evaluating and managing children with CMT, and approaches in clinical trial design in children with CMT and other rare forms of NMD.

Add to Calendar3/15/2022 10:30 AM3/15/2022 12:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Facilitating Multi-Practice Collaboration to Optimize Patient Care

(CME Accredited Session)
Speaker ImageLora Clawson, MSN, CRNP (Chair)

Add to Calendar3/15/2022 10:30 AM3/15/2022 12:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
12:00 PM – 01:30 PM

Industry Forum Lunch Sponsored by Genentech
Industry Forum Lunch Sponsored by PTC
Industry Forum Lunch Sponsored by Sarepta

Add to Calendar3/15/2022 12:00 PM3/15/2022 01:30 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
1:30 PM – 2:30 PM

Building MD Team in NMD

(CME Accredited Session)
Speaker ImageYaacov Anziska, MD (Chair)

Add to Calendar3/15/2022 1:30 PM3/15/2022 02:30 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
1:30 PM – 2:30 PM

Mental Health Support for Clinicians

(CME Accredited Session)
Speaker ImageDeidre Devier, PhD (Chair)


Session will cover the topics of compassion fatigue, compassion, and resilience.

Add to Calendar3/15/2022 1:30 PM3/15/2022 02:30 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
1:30 PM – 3:30 PM

Evolution Ultra-Rare Disease Clinical Trial Design

Speaker ImageDiana Barucha-Goebel, MD (Chair)

Add to Calendar3/15/2022 04:00 PM3/15/2022 06:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Progress in Brain Interface Technology

Add to Calendar3/15/2022 04:00 PM3/15/2022 06:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Treatment Decisions for Disorders with Multiple Therapies

(CME Accredited Session)
Speaker ImageJulie Parsons, MD (Chair)


In this session we will discuss FDA approved therapies for SMA, DMD, ALS, and MG. Strategies for medial decision making and treatment selection will be reviewed.

Add to Calendar3/15/2022 1:30 PM3/15/2022 03:30 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
4:00 PM - 6:00 PM

CRISPR – The Next Generation

Personalized Medicine/Regulatory Approaches for Rare Disease

Speaker ImageTeepu Siddique, MD (Chair)

Add to Calendar3/15/2022 04:00 PM3/15/2022 06:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Impact of Gene Transfer Therapy on Long-Term Multidisciplinary Care

(CME Accredited Session)

Add to Calendar3/15/2022 04:00 PM3/15/2022 06:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online

Business Operations for NMD Clinics

(CME Accredited Session)


Four clinicians will provide their perspective including costs, reimbursement, obtaining assistance and grant funding, hurdles, research, the role of telemedicine, altruism, and future recommendations.

Add to Calendar3/15/2022 04:00 PM3/15/2022 06:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
6:00 PM - 8:00 PM

Exhibits & Poster Networking Reception (Exhibit Hall)

Add to Calendar3/15/2022 6:00 PM3/15/2022 08:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
8:30 AM – 11:00 AM

Clinical Trial Presentations

Add to Calendar3/16/2022 08:30 PM3/16/2022 11:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online
11:30 AM - 3:00 PM

Clinical Trial Presentations

Add to Calendar3/16/2022 11:30 PM3/16/2022 03:00 PMAmerica/Mexico_CityExhibit Hall OpenClick here to join the virtual summit: https://2022mdavirtualconference.org/Online